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Recruiting NCT06057948

A Study of a Vaccine in Combination With Beta-glucan in People With Neuroblastoma

Phase II Interventional Neuroblastoma High-risk Neuroblastoma Metastatic Neuroblastoma

For patients and families

In plain language

An automatic summary of structured registry data. It is an orientation aid, not a substitute for the official protocol or a physician assessment.

What is being studied
The protocol lists: OPT-821 (QS-21), oral β-glucan.
Who it may be relevant to
Registry conditions: Neuroblastoma, High-risk Neuroblastoma, Metastatic Neuroblastoma. Basic parameters: No limits · All.
What needs checking
Age, condition and sex are only basic indicators. Prior treatment, laboratory values and other mandatory requirements appear in the eligibility criteria below.
Where it takes place
United States
Next step
Save the trial, show it to the treating physician, and confirm current recruitment with the study center. Costs, documents and travel →
Official title

Phase II Trial of a Bivalent Vaccine With the Immunological Adjuvant OPT-821 (QS-21), in Combination With Randomization of Oral β-glucan, for High-Risk Neuroblastoma

Overview

The purpose of this study is to test which treatment schedule of β-glucan with bivalent vaccine is more effective for participants with high-risk neuroblastoma that is in complete remission.

Interventions

  • Biological OPT-821 (QS-21)
    Comprised of the immunological adjuvant OPT-821 (QS-21)
  • Dietary supplement oral β-glucan
    Participants will be randomized to receive this agent in two different schedules

Primary outcome measures

  • Mean antibody titer in ng/ml of anti-GD2 IgG1 titer [Time frame: up to 32 weeks]

Eligibility criteria

Inclusion criteria

  • Diagnosis of NB as defined by international criteria,102 i.e., histopathology (confirmed by the MSK Department of Pathology) or BM metastases plus high urine catecholamine levels, or positivity in MIBG scan.
  • HR-NB as defined by risk-related treatment guidelines and international criteria,102 i.e., metastatic/non-localized disease with MYCN amplification (any age), metastatic disease >18 months old, MYCN-amplified localized disease (any age), or disease resistant to standard chemotherapy.
  • HR-NB (as defined above) and in 1) first CR at ≥ 6 months from initiation of immunotherapy using anti-GD2 antibody, or 2) second or subsequent CR (achieved after treatment for PD). CR is defined according to the International Neuroblastoma Response Criteria. Patients with positive MIBG scan but negative FDG-PET scan, and CR in BM, are eligible. For those patients with a positive MIBG scan, the negative FDG-PET scan can be per PI discretion to repeat within the 45 day window period prior to enrollment.
  • Patients with grade 3 toxicities or less using the Common Toxicity Criteria (Version 5.0) developed by the National Cancer Institute of the USA (CTCAE v5.0) related to hematologic, cardiac, neurological, pulmonary, renal, hepatic or gastrointestinal function as determined by blood tests or physical exam. Plus:
  • Absolute neutrophil count (ANC) ≥ 500/mcl
  • Absolute lymphocyte count ≥ 500/mcl
  • >21 and <180 days between completion of systemic therapy and 1st vaccination.
  • A negative pregnancy test is required for patients with child-bearing capability
  • Signed informed consent indicating awareness of the investigational nature of this program.

Exclusion criteria

  • Patients with grade 4 hematologic, cardiac, neurological, pulmonary, renal, hepatic or gastrointestinal function as determined by blood tests or physical exam, using the Common Toxicity Criteria (Version 5.0) developed by the National Cancer Institute of the USA.
  • History of allergy to KLH, QS-21, OPT-821, or glucan
  • Prior treatment with this vaccine.
  • Active life-threatening infection requiring systemic therapy.
  • Inability to comply with protocol requirements.

Criteria are shown verbatim from the registry (in English). Final eligibility is always assessed by the study center.

Healthy volunteers: No

Study design

Allocation
Non-randomized
Model
Parallel assignment
Masking
Open label
Primary purpose
Treatment

Study locations

United States · 7 centers
  • Memorial Sloan Kettering at Basking Ridge (Consent only) — Basking Ridge
  • Memorial Sloan Kettering Monmouth (Consent Only) — Middletown
  • Memorial Sloan Kettering Bergen (Consent Only) — Montvale
  • Memorial Sloan Kettering Suffolk-Commack (Consent only) — Commack
  • Memorial Sloan Kettering Westchester (Consent only) — Harrison
  • Memorial Sloan Kettering Cancer Center (All Protocol Activities) — New York
  • Memorial Sloan Kettering Nassau (Consent Only) — Uniondale

Identifiers

NCT: NCT06057948 · 23-198

Primary sources (government registries)

View this study on ClinicalTrials.gov ↗