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Recruiting NCT04137133

Patienthèque of Finisterian (South of Brittany) Children With Cystic Fibrosis in the Time of Precision Medicine

No phase Interventional Cystic Fibrosis

For patients and families

In plain language

An automatic summary of structured registry data. It is an orientation aid, not a substitute for the official protocol or a physician assessment.

What is being studied
The protocol lists: collection.
Who it may be relevant to
Registry conditions: Cystic Fibrosis. Basic parameters: up to 18 years · All.
What needs checking
Age, condition and sex are only basic indicators. Prior treatment, laboratory values and other mandatory requirements appear in the eligibility criteria below.
Where it takes place
France
Next step
Save the trial, show it to the treating physician, and confirm current recruitment with the study center. Costs, documents and travel →
Official title

Patienthèque of Finisterian (South of Brittany) Children With Cystic Fibrosis in the Time of Precision Medicine.Descriptive Monocentric Study for Identification and Validation of Biomarkers Predictive of Clinical Evolution

Overview

The objective of this study is to evaluate the relevance of Porphyromonas as a biomarker predicting the risk of P. aeruginosa primocolonization in children form 0 to 18 years old with cystic fibrosis.

Detailed description

This is a monocentric study in 3 phases:

* Pre-inclusion: at the first visit to the CRCM (support for a positive screening confirmed by sweat test and genotyping CFTR) * Inclusion: possible between the 2nd visit to the CRCM (about 2 months old) and the 6th month * Follow-up: up to 36 months old. The pace of visits will be based on the usual follow-up rate of CF infants Clinical and paraclinical data and samples will be collected as part of the usual follow-up of CF children. Inclusions and follow-up visits will be carried out at the Roscoff CRCM as well as respiratory explorations and biological samples. Dermatological and odontological follow-ups will be scheduled for each patient at the rate of an annual visit to the CHRU in Brest in the relevant departments.

Interventions

  • Diagnostic test collection
    bronchial secretions, blood, stools, superficial skin sample, dental plaque sample and urine

Primary outcome measures

  • Presence of P. aeruginosa in bacterial sputum cultures in one of bronchial secretions sample [Time frame: 3 years]

Eligibility criteria

Inclusion criteria

  • Newly screened infants with a confirmed diagnosis of cystic fibrosis in its classic form (clinical symptoms and two positive sweat tests and/or two mutations of the cftr gene from Class I to III)
  • Children free of any colonization with P. aeruginosa
  • Affiliation with the social security system
  • Consent signed by the holders of parental authority or the sole parent holding parental authority

Exclusion criteria

  • Children colonized with P. aeruginosa according to the cytobacteriological examination and / or molecular test of sputum or pharyngeal specimens
  • Children grafted
  • Children not affiliated to a social security scheme or not entitled to
  • Children whose parent (s) are (are) minor (s)
  • Children whose holders of parental authority do not master the French language
  • Refusal to participate in the study

Criteria are shown verbatim from the registry (in English). Final eligibility is always assessed by the study center.

Healthy volunteers: No

Study design

Allocation
N/A
Model
Single group
Masking
Open label
Primary purpose
Diagnostic

Study locations

France · 1 center
  • Fondation Ildys — Roscoff

Identifiers

NCT: NCT04137133 · MUCOthèque (29BRC19.0102)

Primary sources (government registries)

View this study on ClinicalTrials.gov ↗